Gene Therapy

CARBON trial: investigating CTX110 allogeneic CRISPR-Cas9–engineered CAR-Ts in R/R LBCL 1:23
CARBON trial: investigating CTX110 allogeneic CRISPR-Cas9–engineered CAR-Ts in R/R LBCL
Constantine Tam • 12 Dec 2022
The safety and efficacy of UCART123v1.2 in R/R AML: results from AMELI-01 2:52
The safety and efficacy of UCART123v1.2 in R/R AML: results from AMELI-01
David Sallman • 11 Dec 2022
Results from a Phase I trial of rapidly manufactured Prgn-3006 Ultracar-T in R/R AML 2:08
Results from a Phase I trial of rapidly manufactured Prgn-3006 Ultracar-T in R/R AML
David Sallman • 11 Dec 2022
Treating otoferlin deficiency with gene therapy 2:51
Treating otoferlin deficiency with gene therapy
Nawal Ouzren • 26 Apr 2022
Novel gene therapy solutions for Usher syndrome type I 2:05
Novel gene therapy solutions for Usher syndrome type I
Nawal Ouzren • 26 Apr 2022
Developing gene therapies for GJB2 gene related hearing loss 1:59
Developing gene therapies for GJB2 gene related hearing loss
Nawal Ouzren • 26 Apr 2022
Implementing automation technology in the CGT space 1:28
Implementing automation technology in the CGT space
Saskia Rösch • 6 Apr 2022
Applications of stem cell gene therapy beyond genetic diseases 1:04
Applications of stem cell gene therapy beyond genetic diseases
Luigi Naldini • 7 Apr 2022
Innovations in treating rare diseases with gene therapies 2:12
Innovations in treating rare diseases with gene therapies
John Maslowski • 27 Jan 2022
Overcoming manufacturing issues in gene therapies for rare diseases 1:38
Overcoming manufacturing issues in gene therapies for rare diseases
John Maslowski • 27 Jan 2022
Meeting the growing demand for gene therapy manufacturing 1:36
Meeting the growing demand for gene therapy manufacturing
John Maslowski • 27 Jan 2022
Addressing immunogenic barriers facing CRISPR-Cas9-based therapies 3:52
Addressing immunogenic barriers facing CRISPR-Cas9-based therapies
Lena Peter • 1 Apr 2022
OTL-103: An autologous gene therapy for Wiskott Aldrich syndrome 1:29
OTL-103: An autologous gene therapy for Wiskott Aldrich syndrome
Kent Christopherson • 27 Jan 2022
Novel gene therapies for metachromatic leukodystrophy 2:31
Novel gene therapies for metachromatic leukodystrophy
Kent Christopherson • 27 Jan 2022
Tangential Flow Depth Filtration in viral vector manufacturing 3:03
Tangential Flow Depth Filtration in viral vector manufacturing
Rachel Legmann • 27 Jan 2022
OCELLOS: A novel advanced therapy orchestration platform 5:12
OCELLOS: A novel advanced therapy orchestration platform
Arturo Araya • 27 Jan 2022
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